New Reference: Niraparib – Abiraterone for HRR-Deficient Metastatic Castration-Sensitive Prostate Cancer

The addition of niraparib to abiraterone significantly improved progression-free survival in patients with HRR-deficient metastatic prostate cancer. Safety analysis showed higher rates of serious adverse events with the combination therapy, including anemia and hypertension.

  • Study

    Randomized, double-blind, placebo-controlled, phase 3 trial [AMPLITUDE]
    HRR-deficient metastatic castration-sensitive prostate cancer
    Niraparib+Abiraterone (n=348) vs Placebo+Abiraterone (n=348)



  • Efficacy

    Radiographic mPFS among pts wit RBCA alterations: NR vs. 26 mos (niraparib vs. placebo) (HR: 0.52 [0.32-0.72])
    Radiographic mPFS among HRR-deficient: NR vs 29.5 mos (HR 0.63 [0.49-0.80])
    OS among BRCA_altered: HR 0.75 [0.51-1.11]
    OS among HR-deficient: HR 0.79 [0.59-1.04]



  • Safety

    Grade >=3 AEs: anemia (29.1% vs 4.6%), hypertension (26.5% vs 18.4%)
    Treatment-emergent deaths: 14 vs 7
    Discontinuation due to AEs: 43.2% vs 10.3%


  • Nat Med. Published online 7 October 2025

    Efstathiou N, Attard G, Agarwal N New Reference: Niraparib – Abiraterone for HRR-Deficient Metastatic Castration-Sensitive Prostate Cancer

    http://doi.org/10.1038/s41591-025-03961-8

    Reviewed by Ulas D. Bayraktar, MD on Dec 19, 2025

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